The Gene Therapy for CNS Summit is the only industry-led conference focused exclusively on innovating and optimizing gene therapies for Central Nervous System disorders. This dedicated meeting addresses the increasing demand for solutions driven by a changing regulatory landscape, the urgent push to advance first-in-class vector delivery methods through the clinic, and the growing mandate to develop effective gene therapies for rare CNS conditions.

The summit is designed to equip attendees with in-depth, practical content to streamline development and improve efficacy. Key sessions focus on optimizing AAVs, innovating capsids, and developing novel vectors to improve delivery to the brain while enhancing blood-brain barrier crossing to reduce toxicities. Furthermore, the agenda offers essential insights into maximizing translational models for moving from discovery to the clinic, streamlining early-stage manufacturing processes, analyzing different delivery devices, and successfully navigating IND submissions and regulatory guidance to ensure compliance.